Answer: d) Laronidase.
Laronidase is used to treat mucopolysaccharide
storage disorders (specifically mucopolysaccharidosis 1 or Hurlers syndrome)
caused by deficiencies of alpha-L-iduronidase. Reduced or absent
a-L-iduronidase activity results in the accumulation of the GAG substrates,
dermatan sulfate and heparan sulfate, throughout the body and leads to
widespread cellular, tissue, and organ dysfunction.
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